Baixar PDF

Outros usuários também visualizaram estes artigos

EFFICACY AND SAFETY OF VALOCTOCOGENE ROXAPARVOVEC 4 YEARS AFTER GENE TRANSFER IN GENER8-1 MC Ozelo, AD Leavitt, J Mahlangu, G Kenet, SW Pipe, S Chou, R Klamroth, F Peyvandi, T Robinson, GT Group
10.1016/j.htct.2024.09.964
A SIMULATION STUDY TO PROVIDE GUIDANCE FOR INDIVIDUALS TRANSITIONING FROM EMICIZUMAB TO VALOCTOCOGENE ROXAPARVOVEC W Kuwabara, D Osmond, J Henshaw, S Agarwal, V Newman, C Hermans, W Miesbach, S Pipe, RS Jr, F Peyvandi
10.1016/j.htct.2023.09.840
HEALTH-RELATED QUALITY-OF-LIFE OUTCOMES 4-YEARS AFTER TREATMENT WITH VALOCTOCOGENE ROXAPARVOVEC FP Careta, B Madan, MC Ozelo, G Kenet, S Chou, S Pipe, A Leavitt, A Ruiz, E Dashiell-Aje, J Mahlangu
10.1016/j.htct.2024.09.972