TY - JOUR T1 - A PHASE 1/2 OPEN LABEL EXTENSION STUDY OF GIVOSIRAN, AN INVESTIGATIONAL RNAI THERAPEUTIC, IN PATIENTS WITH ACUTE INTERMITTENT PORPHYRIA JO - Hematology, Transfusion and Cell Therapy T2 - AU - Marchi,R. AU - Duarte,L. AU - P,S. AU - D,R. AU - Ke,A. AU - Hl,B. AU - E,S. AU - P,H. AU - M,B. AU - Al,E. SN - 25311379 M3 - 10.1016/j.htct.2020.10.028 DO - 10.1016/j.htct.2020.10.028 UR - http://www.htct.com.br/en-a-phase-1-2-open-label-articulo-S253113792030314X ER -